Gene therapy

Accelerating gene therapy: assessment and prospects at the end of the DIM Gene Therapy program

First in vivo success of a gene therapy for the maple syrup urine disease

A new tool to correct a mutation in beta-thalassemia

JOB OFFER – 18 months postdoctoral position in Imagine Institute: AAV gene therapy for Maple Syrup Urine Disease (MSUD)

First successes and new approaches in gene therapy

A201701 – Gene therapy of auditory damage

Christine Petit

D201703 – New gene therapy strategy for sickle cell disease using umbilical cord blood

Anne Galy

D201702 – Preclinical development of new lentiviral vectors and gene therapy strategies to treat sickle cell disease

Annarita Miccio

D201701- Development of new therapeutic strategies in sickle cell disease

Pr. Pablo Bartolucci