
Gene therapy
Accelerating gene therapy: assessment and prospects at the end of the DIM Gene Therapy program

Gene therapyInborn Errors of MetabolismMSUD
The DIM « thérapie génique » aims to federate them and accelerate the development of gene therapy to reinforce, in the light of personalized medicine, it grades among the most promising and innovative therapeutic strategies. This initiative aims to provide treatment for serious or chronic pathologies without treatment till today, or for which the medical care is still largely not satisfying.